TABLE 1

Patient Characteristics

CharacteristicData
Participants 19
Age (mo)8.3 (4.0–22.0)
Age at diagnosis (d)7 (1.5–12)
Sex
 Female8/19 (42%)
 Male11/19 (58%)
Genetic mutation
 Paternal ABCC8 mutation16/19 (84%)
 No or unknown mutation3/19 (16%)
Response to medication
 Full5/19 (26%)
 Partial14/19 (74%)
  • Qualitative data are number and percentage; continuous data are median and interquartile range.