Patient Characteristics
Characteristic | Data |
---|---|
Participants | 19 |
Age (mo) | 8.3 (4.0–22.0) |
Age at diagnosis (d) | 7 (1.5–12) |
Sex | |
Female | 8/19 (42%) |
Male | 11/19 (58%) |
Genetic mutation | |
Paternal ABCC8 mutation | 16/19 (84%) |
No or unknown mutation | 3/19 (16%) |
Response to medication | |
Full | 5/19 (26%) |
Partial | 14/19 (74%) |
Qualitative data are number and percentage; continuous data are median and interquartile range.